MPS II Immunophenotyping

Key facts

Sponsor

Duke University

Principal Investigator

Priya Kishnani, MD

Duke University

Enrollment

6 enrolled

Eligibility

All sexes

Timeline

2022 – 2024

Study locations (1)

• Duke University, Durham, North Carolina, United States

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Other trials for Mucopolysaccharidosis

Additional recruiting or active studies for the same condition.

• ENROLLING BY INVITATIONPHASE2, PHASE3NCT06075537
  An Extension Study of the Long-Term Safety, Tolerability, and Efficacy of Tividenofusp Alfa (DNL310) in Participants With Mucopolysaccharidosis Type II (MPS II) From Study DNLI-E-0002 or Study DNLI-E-0007
  Denali Therapeutics Inc.
• ENROLLING BY INVITATIONNCT06103487
  Long Term Follow-Up for RGX-111
  REGENXBIO Inc.
• RECRUITINGPHASE1NCT05682144
  ISP-001: Sleeping Beauty Transposon-Engineered B Cells for MPS I
  Immusoft of CA, Inc.
• ENROLLING BY INVITATIONPHASE3NCT05594992
  An Extension Study of JR-141 to Evaluate the Long-term Safety and Efficacy in MPS II (Hunter Syndrome) Subjects
  JCR Pharmaceuticals Co., Ltd.
• ACTIVE NOT RECRUITINGPHASE1NCT05422482
  A Study to Evaluate the Safety, Tolerability, PK and PD of Intracerebroventricular GC1123 in Patients with MPS Ⅱ
  GC Biopharma Corp
• RECRUITINGPHASE2, PHASE3NCT05371613
  A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II)
  Denali Therapeutics Inc.
• RECRUITINGNANCT05619900
  Registry of Patients Diagnosed With Lysosomal Storage Diseases
  University of California, San Francisco
• ACTIVE NOT RECRUITINGPHASE3NCT04573023
  A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT)
  JCR Pharmaceuticals Co., Ltd.

See all trials for Mucopolysaccharidosis →