Active, not recruitingPhase 3NCT04910776
Clinical Study for Treatment-naïve IOPD Babies to Evaluate Efficacy and Safety of ERT With Avalglucosidase Alfa
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Sanofi
- Principal Investigator
- Clinical Sciences & OperationsSanofi
- Intervention
- avalglucosidase alfa(drug)
- Enrollment
- 17 enrolled
- Eligibility
- All sexes
- Timeline
- 2021 – 2027
Study locations (16)
- Stanford Hospital- Site Number : 8400006, Stanford, California, United States
- Children's Hospitals and Clinics of Minnesota- Site Number : 8400008, Minneapolis, Minnesota, United States
- Advanced Medical Genetics- Site Number : 8400002, Hawthorne, New York, United States
- Duke University Medical Center- Site Number : 8400004, Durham, North Carolina, United States
- Cincinnati Children's Hospital Medical Center- Site Number : 8400001, Cincinnati, Ohio, United States
- Seattle Children's Hospital- Site Number : 8400003, Seattle, Washington, United States
- Investigational Site Number : 0560001, Leuven, Belgium
- Investigational Site Number : 1560002, Qingdao, China
- Investigational Site Number : 1560001, Shanghai, China
- Investigational Site Number : 2760001, Bad Oeynhausen, Germany
- Investigational Site Number : 3800002, Monza, Lombardy, Italy
- Investigational Site Number : 5280001, Rotterdam, Netherlands
- Investigational Site Number : 7240001, Esplugues de Llobregat, Catalunya [Cataluña], Spain
- Investigational Site Number : 1580001, Taipei, Taiwan
- Investigational Site Number : 8260001, London, London, City of, United Kingdom
- +1 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT04910776 on ClinicalTrials.govOther trials for Glycogen storage disease due to acid maltase deficiency
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