Active, not recruitingNCT04848779
A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients ≤6 Months of Age With Infantile-onset Pompe Disease (IOPD)
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Sanofi
- Principal Investigator
- Clinical Sciences & OperationsSanofi
- Intervention
- Alglucosidase alfa GZ419829(drug)
- Enrollment
- 16 enrolled
- Eligibility
- All sexes
- Timeline
- 2021 – 2026
Study locations (15)
- Advanced Medical Genetics- Site Number : 8400002, Hawthorne, New York, United States
- Duke University Medical Center- Site Number : 8400004, Durham, North Carolina, United States
- Cincinnati Children's Hospital Medical Center- Site Number : 8400001, Cincinnati, Ohio, United States
- Le Bonheur Children's Hospital- Site Number : 8400005, Memphis, Tennessee, United States
- Seattle Children's Hospital- Site Number : 8400003, Seattle, Washington, United States
- Investigational Site Number : 0560001, Leuven, Belgium
- Investigational Site Number : 2500001, Tours, France
- Investigational Site Number : 2760001, Giessen, Germany
- Investigational Site Number : 3800002, Monza, Monza E Brianza, Italy
- Investigational Site Number : 3800001, Florence, Italy
- Investigational Site Number : 5280001, Rotterdam, Netherlands
- Investigational Site Number : 7240001, Esplugues de Llobregat, Catalunya [Cataluña], Spain
- Investigational Site Number : 1580001, Taipei, Taiwan
- Investigational Site Number : 8260001, London, London, City of, United Kingdom
- Investigational Site Number : 8260002, Manchester, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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