Cognitive and Neurological Pathologies in Pompe Disease

Key facts

Sponsor

Duke University

Principal Investigator

Priya Kishnani, MD

Duke University

Enrollment

45 enrolled

Eligibility

0-18 years · All sexes

Timeline

2016 – 2029

Study locations (1)

• Duke University Medical Center, Durham, North Carolina, United States

Collaborators

Sanofi

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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