Long-term Efficacy of Carglumic Acid in Organic Acidemia.

Key facts

Sponsor

National Taiwan University Hospital

Principal Investigator

Ni-Chung Lee, M.D., Ph.D

National Taiwan University Hospital

Intervention

Carglumic Acid (Carbaglu®)(drug)

Enrollment

3 enrolled

Eligibility

0-18 years · All sexes

Timeline

2019 – 2025

Study locations (1)

• National Taiwan University Hospital, Taipei, Taiwan

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Other trials for Disorder of branched-chain amino acid metabolism

Additional recruiting or active studies for the same condition.

• RECRUITINGNANCT07573059
  Evaluation of the Safety of Loargys Arginine Test System in Loargys-treated Patients
  Immedica Pharma US Inc
• ENROLLING BY INVITATIONNANCT06953505
  At Home Ammonia Monitoring of Inborn Errors of Ammonia Metabolism
  Sequitur Health Corp.
• RECRUITINGNCT05040178
  An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
  RECORDATI GROUP
• RECRUITINGPHASE1, PHASE2NCT05130437
  A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
  ModernaTX, Inc.
• RECRUITINGPHASE1, PHASE2NCT04159103
  Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
  ModernaTX, Inc.
• RECRUITINGNCT04176523
  Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach
  RECORDATI GROUP
• RECRUITINGNCT02890342
  Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
  National Human Genome Research Institute (NHGRI)

See all trials for Disorder of branched-chain amino acid metabolism →