RecruitingNCT04176523
Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach
Studying Disorder of branched-chain amino acid metabolism
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- RECORDATI GROUP
- Principal Investigator
- Sufin Yap, MDSheffield Children's NHS Trust
- Intervention
- Carglumic Acid(drug)
- Enrollment
- 95 enrolled
- Eligibility
- 99 years · All sexes
- Timeline
- 2019 – 2029
Study locations (30)
- Hopital Des Enfants, CHU de Bordeaux-GH Pellegrin, Bordeaux, France
- Hopital de la Conception, Marseille, France
- Hôpital de la Timone, Marseille, France
- CHU de Nancy - Hopitaux de Brabois, Nancy, France
- Hôpital Necker Enfants Malades, Paris, France
- CHU de Rouen, Rouen, France
- Nouvel Hopital Civil, Strasbourg, France
- Hopital de Hautepierre, Strasbourg, France
- Klinikum Bremen Mitte, Prof. Hess Kinderklinik, Bremen, Germany
- Azienda Ospedaliero Universitaria Meyer, Florence, Italy
- San Paola Hospital, ASST Santi Paolo e Carlo, Milan, Italy
- Milan Policlinico University, Milan, Italy
- Azienda Ospedaliera San Gerardo Monza, Monza, Italy
- Azienda Ospedaliera Universitaria Federico II, Naples, Italy
- University Hospital of Padova, Padua, Italy
- +15 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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