RecruitingPHASE1, PHASE2NCT04159103
Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
Studying Disorder of branched-chain amino acid metabolism
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- ModernaTX, Inc.
- Intervention
- mRNA-3927(biological)
- Enrollment
- 77 enrolled
- Eligibility
- All sexes
- Timeline
- 2021 – 2027
Study locations (30)
- UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles, California, United States
- Ronald Reagan UCLA Medical Center, Los Angeles, California, United States
- Lucile Packard Children's Hospital Stanford, Stanford, California, United States
- Nicklaus Children's Hospital, Miami, Florida, United States
- University of South Florida - 12901 Bruce B Downs, Tampa, Florida, United States
- Ann and Robert H Lurie Childrens Hospital of Chicago, Chicago, Illinois, United States
- Johns Hopkins Hospital, Adult Outpatient Clinical Research Unit, Baltimore, Maryland, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- University of Michigan Hospitals, Ann Arbor, Michigan, United States
- Icahn School of Medicine at Mount Sinai - Clinical Research Unit, New York, New York, United States
- Duke University Medical System (Duke Health), Durham, North Carolina, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- University Hospitals Cleveland Medical Center - 11100 Euclid Ave, Cleveland, Ohio, United States
- Children's Hospital of Philadelphia (CHOP), Philadelphia, Pennsylvania, United States
- Texas Children's Hospital, Houston, Texas, United States
- +15 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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