RecruitingNCT05040178
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
Studying Disorder of branched-chain amino acid metabolism
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- RECORDATI GROUP
- Principal Investigator
- William Ludlum, MDRecordati Rare Diseases Inc
- Intervention
- Carglumic Acid(drug)
- Enrollment
- 20 enrolled
- Eligibility
- All sexes
- Timeline
- 2022 – 2032
Study locations (5)
- Children's National Hospital, Washington D.C., District of Columbia, United States
- University of South Florida, Tampa, Florida, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- Riley Children's Hospital, Indianapolis, Indiana, United States
- Icahn School of Medicine at Mt. Sinai, New York, New York, United States
Collaborators
Target PharmaSolutions, Inc.
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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