Active, not recruitingPHASE1, PHASE2NCT04093349
A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Spark Therapeutics, Inc.
- Principal Investigator
- Tahseen Mozaffar, MDUniversity of California Irvine Health
- Intervention
- SPK-3006(genetic)
- Enrollment
- 4 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2020 – 2032
Study locations (29)
- Barrow Neurological Institute, Phoenix, Arizona, United States
- University of California Irvine Health, Orange, California, United States
- Emory University School of Medicine, Atlanta, Georgia, United States
- University of Kansas Medical Center Research Institute, Kansas City, Kansas, United States
- University of Minnesota, Minneapolis, Minnesota, United States
- Oregon Health & Science University, Portland, Oregon, United States
- University of Pennsylvania, Philadelphia, Pennsylvania, United States
- University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania, United States
- University of Utah, Salt Lake City, Utah, United States
- Lysosomal and Rare Disorders Research & Treatment Center, Fairfax, Virginia, United States
- Vancouver General Hospital, Vancouver, British Columbia, Canada
- The Ottawa Hospital, Ottawa, Ontario, Canada
- Montreal Neurological Hospital, Montreal, Quebec, Canada
- Rigshospitalet, Copenhagen, Denmark
- Centre Hospitalier Universitaire d'Angers, Angers, France
- +14 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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