CompletedPHASE1, PHASE2NCT04018755
Open-label Study of Anakinra in MPS III
Studying Mucopolysaccharidosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Lynda E Polgreen
- Principal Investigator
- Lynda Polgreen, MD, MSThe Lundquist Institute at Harbor-UCLA Medical Center
- Intervention
- anakinra(biological)
- Enrollment
- 24 enrolled
- Eligibility
- 4 years · All sexes
- Timeline
- 2020 – 2023
Study locations (1)
- The Lundquist Institute at Harbor-UCLA Medical Center, Torrance, California, United States
Collaborators
Cure Sanfilippo Foundation · Swedish Orphan Biovitrum
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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