Active, not recruitingPhase 3NCT03911505
ZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPD
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Amicus Therapeutics
- Intervention
- Cipaglucosidase Alfa(biological)
- Enrollment
- 21 enrolled
- Eligibility
- 0-17 years · All sexes
- Timeline
- 2020 – 2026
Study locations (17)
- University of Florida Clinical Research Center, Gainesville, Florida, United States
- Wolfson Children's Hospital, Jacksonville, Florida, United States
- Woodruff Memorial Research Building, Atlanta, Georgia, United States
- St. Louis Children's Hospital, St Louis, Missouri, United States
- Duke University Medical Center, Durham, North Carolina, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
- University of Utah, Clinical and Translational Sciences Institute, Salt Lake City, Utah, United States
- Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax, Virginia, United States
- Women's and Children's Hospital, North Adelaide, South Australia, Australia
- University of Calgary, Calgary, Alberta, Canada
- SphinCS GmbH Clinical Science for LSD, Hochheim am Main, Hesse, Germany
- San Gerardo Hospital, Monza, Italy
- Izumi City General Hospital, Osaka, Izumi-Shi, Japan
- Gunma University Hospital, Gunma, Japan
- +2 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT03911505 on ClinicalTrials.govOther trials for Glycogen storage disease due to acid maltase deficiency
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