Developing a Management Approach for Patients With "Late-Onset" Pompe Disease

Key facts

Sponsor

Duke University

Principal Investigator

Priya Kishnani, MD

Duke University

Intervention

Observational(other)

Enrollment

20 enrolled

Eligibility

All sexes

Timeline

2019 – 2027

Study locations (1)

• Duke University, Durham, North Carolina, United States

Collaborators

Genzyme, a Sanofi Company

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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