Cardiopulmonary Exercise Test to Quantify Enzyme Replacement Response in Pediatric Pompe Disease

Key facts

Sponsor

Rambam Health Care Campus

Principal Investigator

Lea Bentur, Prof.

Rambam Health Care Campus

Enrollment

5 enrolled

Eligibility

8 years · All sexes

Timeline

2014 – 2017

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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