Active, not recruitingPhase 2NCT03019406
A Study to Assess Safety and Efficacy of Avalglucosidase Alfa Administered Every Other Week in Pediatric Patients With Infantile-onset Pompe Disease Previously Treated With Alglucosidase Alfa
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Genzyme, a Sanofi Company
- Principal Investigator
- Clinical Sciences & OperationsSanofi
- Intervention
- Avalglucosidase alfa (GZ402666)(drug)
- Enrollment
- 22 enrolled
- Eligibility
- 17 years · All sexes
- Timeline
- 2017 – 2027
Study locations (12)
- Regional Medical Genetics Center of New York Site Number : 8400002, Valhalla, New York, United States
- Duke University Medical Center Site Number : 8400001, Durham, North Carolina, United States
- Seattle Childrens Hospital and Regional Medical Center- Site Number : 8400005, Seattle, Washington, United States
- Investigational Site Number : 2500004, Nantes, France
- Investigational Site Number : 2500003, Paris, France
- Investigational Site Number : 2500002, Paris, France
- Investigational Site Number : 2500001, Tours, France
- Investigational Site Number : 3920001, Fuchu-shi, Tokyo, Japan
- Investigational Site Number : 3920002, Fuchu-shi, Tokyo, Japan
- Investigational Site Number : 1580001, Hsinchu, Taiwan
- Investigational Site Number : 8260001, London, London, City of, United Kingdom
- Investigational Site Number : 8260002, Manchester, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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