TerminatedPHASE1, PHASE2NCT02898753
VAL-1221 Delivered Intravenously in Ambulatory and Ventilator-free Participants With Late-Onset Pompe Disease
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Valerion Therapeutics, LLC
- Principal Investigator
- Hal Landy, MDValerion Therapeutics, LLC
- Intervention
- VAL-1221(drug)
- Enrollment
- 12 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2017 – 2020
Study locations (3)
- University of California, Irvine, Orange, California, United States
- Duke University Medical Center, Durham, North Carolina, United States
- National Hospital for Neurology and Neurosurgery, London, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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