Investigating Pompe Prevalence in Neuromuscular Medicine Academic Practices

Key facts

Sponsor

University of California, Irvine

Principal Investigator

Tahseen Mozaffar, MD

University of California, Irvine

Enrollment

921 enrolled

Eligibility

8 years · All sexes

Timeline

2015 – 2018

Study locations (1)

• University of California, Irvine, Irvine, California, United States

Collaborators

Genzyme, a Sanofi Company

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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See all trials for Glycogen storage disease due to acid maltase deficiency →