CompletedPHASE2, PHASE3NCT02612129
Arimoclomol Prospective Study in Participants Diagnosed With Niemann-Pick Disease Type C
Studying Niemann-Pick disease type C
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- ZevraDenmark
- Principal Investigator
- Karl-Eugen MengelSphinCS GmbH, Hochheim, Germany
- Intervention
- arimoclomol(drug)
- Enrollment
- 50 enrolled
- Eligibility
- 2-18 years · All sexes
- Timeline
- 2016 – 2024
Study locations (14)
- UCSF Benioff Children's Hospital Oakland, Oakland, California, United States
- Mayo Clinic Children's Center, Rochester, Minnesota, United States
- University Hospital Copenhagen (Rigshospitalet), Copenhagen, Denmark
- CHU de Montpellier, Montpellier, France
- Hôpital Trousseau, Paris, France
- Villa Metabolica, Universitätsmedizin Mainz, Mainz, Germany
- Dr. von Haunersches Kinderspital der Universität München, Munich, Germany
- Ospedale Pediatrico Bambino Gesù, Rome, Italy
- Azienda Ospedaliero-Universitaria "Santa Maria della Misericordia" di Udin, Udine, Italy
- The Children´s Memorial Istitute Warsaw, Warsaw, Poland
- Hospital Vall D'Hebron, Barcelona, Spain
- INSELSPITAL University Hospital Bern, Bern, Switzerland
- Birmingham Children's Hospital, Birmingham, United Kingdom
- Great Ormond Street Hospital, London, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT02612129 on ClinicalTrials.govOther trials for Niemann-Pick disease type C
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