Active, not recruitingPhase 3NCT04860960
Phase 3 Study to Evaluate Intravenous Trappsol(R) Cyclo(TM) in Pediatric and Adult Patients With Niemann-Pick Disease Type C1
Studying Niemann-Pick disease type C
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Cyclo Therapeutics, Inc.
- Principal Investigator
- Karen Mullen, MDCyclo Therapeutics, Inc.
- Intervention
- Hydroxypropyl-beta-cyclodextrin(drug)
- Enrollment
- 94 enrolled
- Eligibility
- 3 years · All sexes
- Timeline
- 2021 – 2026
Study locations (30)
- UCSF Benioff Children's Hospital Oakland, Oakland, California, United States
- University of Florida, Jacksonville, Florida, United States
- Emory, Atlanta, Georgia, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- UPMC Children's Hospital, Pittsburgh, Pennsylvania, United States
- University Utah, Salt Lake City, Utah, United States
- Lysosomal and Rare Disorders Research & Treatment Center, Inc., Fairfax, Virginia, United States
- Hospital de Alta Complejidad en Red "El Cruce", Buenos Aires, Argentina
- Hospital de Niños de la Santísima Trinidad, Córdoba, Argentina
- Melbourne Children's Trials Centre Murdoch Children's Research Institute, Parkville, Victoria, Australia
- Royal Melbourne Hospital, Parkville, Victoria, Australia
- Metabolic Clinical Trials Unit, Adelaide, Australia
- Hospital de Clínicas de Porto Alegre, Porto Alegre, Brazil
- Universidade de São Paulo, São Paulo, Brazil
- University of Campinas, São Paulo, Brazil
- +15 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT04860960 on ClinicalTrials.govOther trials for Niemann-Pick disease type C
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- RECRUITINGNANCT00344331Evaluation of Biochemical Markers and Clinical Investigation of Niemann-Pick Disease, Type CEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)