Clinical trials for Niemann-Pick disease type C
4 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGN/ANCT05588167Establishment of Genomic and Phenotypic Database for Niemann-Pick Disease, Type CEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) · PI: Forbes D Porter, M.D.
- RECRUITINGPhase 3NCT05163288A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type CIntraBio Inc
- ACTIVE NOT RECRUITINGPhase 3NCT04860960Phase 3 Study to Evaluate Intravenous Trappsol(R) Cyclo(TM) in Pediatric and Adult Patients With Niemann-Pick Disease Type C1Cyclo Therapeutics, Inc. · PI: Karen Mullen, MD
- RECRUITINGN/ANCT00344331Evaluation of Biochemical Markers and Clinical Investigation of Niemann-Pick Disease, Type CEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) · PI: Forbes D Porter, M.D.