RecruitingPhase 3NCT05163288
A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C
Studying Niemann-Pick disease type C
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- IntraBio Inc
- Intervention
- N-Acetyl-L-Leucine(drug)
- Enrollment
- 53 enrolled
- Eligibility
- 4 years · All sexes
- Timeline
- 2022 – 2028
Study locations (14)
- Mayo Clinic, Rochester, Minnesota, United States
- The Royal Melbourne Hospital, Parkville, Victoria, Australia
- First Faculty of Medicine, Charles University Hospital Prague, Prague, Czechia
- University of Giessen, Giessen, Germany
- University of Hamburg, Hamburg, Germany
- SphinCS - Institute of Clinical Science in Lysosomal Storage Disorders, Höchheim, Germany
- Ludwig Maximilian University of Munich, München, Germany
- University Hospital Münster, Münster, Germany
- Amsterdam UMC, Amsterdam, Netherlands
- Comenius University in Bratislva, Bratislava, Slovakia
- University Hospital Bern Inselspital, Bern, Switzerland
- Great Ormond Street Hospital, London, United Kingdom
- Royal Free London NHS Foundation Trust, London, United Kingdom
- Royal Manchester Children's Hospital, Manchester, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT05163288 on ClinicalTrials.govOther trials for Niemann-Pick disease type C
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