UnknownPHASE1, PHASE2NCT02559830

Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy

Studying Metachromatic leukodystrophy

Last synced from ClinicalTrials.gov

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Key facts

Sponsor
Shenzhen Second People's Hospital
Principal Investigator
Qizhou Lian, M.D.,Ph.D.
The University of Hong Kong
Intervention
transduced CD34+ hematopoietic stem cell(genetic)
Enrollment
50 enrolled
Eligibility
1-16 years · All sexes
Timeline
20152025

Study locations (1)

Collaborators

Shenzhen University · Guangzhou Women and Children's Medical Center

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT02559830 on ClinicalTrials.gov

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