RecruitingNot applicableNCT07046338
Lentiviral Hematopoietic Stem Cell Gene Therapy for MLD
Studying Metachromatic leukodystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Shenzhen Geno-Immune Medical Institute
- Principal Investigator
- Lung-Ji Chang, Ph.D
- Intervention
- Lentiviral TYF-ARSA correction of patient's autologous HSCs(genetic)
- Enrollment
- 10 enrolled
- Eligibility
- 1-50 years · All sexes
- Timeline
- 2025 – 2025
Study locations (1)
- Shenzhen Geno-Immune Medical Institute, Shenzhen, Guangdong, China
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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