Active, not recruitingPhase 3NCT04283227
OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)
Studying Metachromatic leukodystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Orchard Therapeutics
- Principal Investigator
- Orchard Clinical TrialsOrchard Therapeutics
- Intervention
- OTL-200(genetic)
- Enrollment
- 6 enrolled
- Eligibility
- All sexes
- Timeline
- 2022 – 2031
Study locations (1)
- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET), Milan, Italy
Collaborators
Ospedale San Raffaele
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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