Clinical trials for Metachromatic leukodystrophy
7 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGN/ANCT07046338Lentiviral Hematopoietic Stem Cell Gene Therapy for MLDShenzhen Geno-Immune Medical Institute · PI: Lung-Ji Chang, Ph.D
- RECRUITINGN/ANCT03725670Direct Lentiviral Injection Gene Therapy for MLDShenzhen Geno-Immune Medical Institute · PI: Lung-Ji Chang, Ph.D
- ACTIVE NOT RECRUITINGPhase 3NCT04283227OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)Orchard Therapeutics · PI: Orchard Clinical Trials
- RECRUITINGNCT04925349Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaAssistance Publique - Hôpitaux de Paris · PI: Fanny MOCHEL, MCU-PH
- ACTIVE NOT RECRUITINGPhase 2NCT03771898A Study of Intrathecal SHP611 in Children With Metachromatic LeukodystrophyShire · PI: Study Director
- ACTIVE NOT RECRUITINGPhase 2NCT02171104MT2013-31: Allo HCT for Metabolic Disorders and Severe OsteopetrosisMasonic Cancer Center, University of Minnesota · PI: Paul Orchard, M.D.
- RECRUITINGNCT03333200Longitudinal Study of Neurodegenerative DisordersUniversity of Pittsburgh