Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia

Key facts

Sponsor

King Abdullah International Medical Research Center

Principal Investigator

Majid A. Alfadhel, MD, M.D

King Abdulaziz Medical City, National Guard / Riyadh-Saudi Arabia

Intervention

Carglumic Acid(drug)

Enrollment

33 enrolled

Eligibility

15 years · All sexes

Timeline

2015 – 2019

Study locations (2)

• King Abdullah Specialist Children Hospital, King Abdulaziz Medical City, Riyadh, Saudi Arabia
• King Fahad Medical City, Riyadh, Saudi Arabia

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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