A Pilot Study of Pyridostigmine in Pompe Disease

Key facts

Sponsor

University of Florida

Principal Investigator

Barry J Byrne, MD, PhD

University of Florida

Intervention

Pyridostigmine Bromide(drug)

Enrollment

2 enrolled

Eligibility

8-60 years · All sexes

Timeline

2015 – 2018

Study locations (1)

• University of Florida Clinical Research Center, Gainesville, Florida, United States

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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