UnknownNCT01914536
A Natural History Study of Adult Onset Pompe Disease Using Muscle MRI
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau
- Principal Investigator
- Jordi Díaz Manera, MD PhDFundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau
- Enrollment
- 30 enrolled
- Eligibility
- 8 years · All sexes
- Timeline
- 2013 – 2017
Study locations (1)
- Hospital de la Santa Creu iSant Pau, Barcelona, Barcelona, Spain
Collaborators
Genzyme, a Sanofi Company
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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