Safety and Efficacy of Albuterol in Individuals With Late-onset Pompe Disease

Key facts

Sponsor

Duke University

Principal Investigator

Dwight d Koeberl, MD, PhD

Duke University

Intervention

Albuterol(drug)

Enrollment

16 enrolled

Eligibility

18 years · All sexes

Timeline

2013 – 2016

Study locations (1)

• Duke University Medical Center, Durham, North Carolina, United States

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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