Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia

Key facts

Sponsor

Mendel Tuchman

Principal Investigator

Mendel Tuchman, MD

Children's National Research Institute

Intervention

N-carbamylglutamate(drug)

Enrollment

1 enrolled

Eligibility

All sexes

Timeline

2012 – 2015

Study locations (7)

• University of California Los Angeles, Los Angeles, California, United States
• Lucile Packard Children's Hospital at Stanford, Palo Alto, California, United States
• The Children's Hospital of Colorado, Aurora, Colorado, United States
• Children's National Medical Center, Washington D.C., District of Columbia, United States
• Children's Hospital Boston, Boston, Massachusetts, United States
• University Hospitals of Cleveland/Rainbow Babies and Children's Hospital, Cleveland, Ohio, United States
• The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

Collaborators

Children's National Research Institute · Boston Children's Hospital · University Hospitals Cleveland Medical Center · University of California, Los Angeles · Children's Hospital of Philadelphia · Lucile Packard Children's Hospital · University of Colorado, Denver

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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