Observational Study for Subjects With Pompe Disease Undergoing Immune Modulation Therapies

Key facts

Sponsor

University of Florida

Principal Investigator

Barry J Byrne, MD, PhD

University of Florida

Intervention

Rituximab(drug)

Enrollment

11 enrolled

Eligibility

65 years · All sexes

Timeline

2008 – 2017

Study locations (1)

• University of Florida, Gainesville, Florida, United States

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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