CompletedPhase 3NCT01415427

Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)

Studying Mucopolysaccharidosis

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Key facts

Sponsor
BioMarin Pharmaceutical
Principal Investigator
Debra Lounsbury
BioMarin Pharmaceutical
Intervention
BMN 110 - Weekly(drug)
Enrollment
173 enrolled
Eligibility
5 years · All sexes
Timeline
20112016

Study locations (30)

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT01415427 on ClinicalTrials.gov

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