CompletedPhase 2NCT01303146
Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation
Studying Metachromatic leukodystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Assistance Publique - Hôpitaux de Paris
- Principal Investigator
- Patrick Aubourg, MD, PhDDepartment of Pediatric Endocrinology and Neurology, Saint Vincent de Paul Hospital, Paris
- Intervention
- rhARSA(drug)
- Enrollment
- 1 enrolled
- Eligibility
- All sexes
- Timeline
- 2008 – 2010
Study locations (1)
- Department of Pediatric Endocrinology and Neurology, Saint Vincent de Paul Hospital, Paris, France
Collaborators
European Leukodystrophy Association · Zymenex A/S · Shire · URC-CIC Paris Descartes Necker Cochin
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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