Genotype-Phenotype Correlations of Late Infantile Neuronal Ceroid Lipofuscinosis

Key facts

Sponsor

Weill Medical College of Cornell University

Principal Investigator

Ronald G. Crystal, MD, MD

Weill Medical College of Cornell University

Enrollment

48 enrolled

Eligibility

2-18 years · All sexes

Timeline

2009 – 2016

Study locations (1)

• Weill Cornell Medicine, New York, New York, United States

Collaborators

Rare Diseases Clinical Research Network · National Institute of Neurological Disorders and Stroke (NINDS) · National Institutes of Health (NIH)

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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