CompletedPHASE1, PHASE2NCT00976352
Safety Study of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase to Treat Pompe Disease
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- University of Florida
- Principal Investigator
- Barry J Byrne, MD, PhDUniversity of Florida
- Intervention
- rAAV1-CMV-GAA (study agent) Administration(drug)
- Enrollment
- 9 enrolled
- Eligibility
- 2-18 years · All sexes
- Timeline
- 2010 – 2015
Study locations (1)
- Shands at the University of Florida, Gainesville, Florida, United States
Collaborators
National Heart, Lung, and Blood Institute (NHLBI)
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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