Anaplerotic Therapy in Propionic Acidemia

Key facts

Sponsor

Nicola Longo

Principal Investigator

Nicola Longo, MD, PhD

University of Utah

Intervention

ornithine alpha ketoglutarate(drug)

Enrollment

3 enrolled

Eligibility

5-12 years · All sexes

Timeline

2008 – 2010

Study locations (1)

• University of Utah, Department of Pediatrics, Salt Lake City, Utah, United States

Collaborators

National Institutes of Health (NIH) · National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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