RecruitingNot applicableNCT00231400
Pompe Disease Registry Protocol
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Genzyme, a Sanofi Company
- Principal Investigator
- Study DirectorGenzyme, a Sanofi Company
- Enrollment
- 2000 enrolled
- Eligibility
- All sexes
- Timeline
- 2004 – 2034
Study locations (20)
- University Alabama at Birmingham- Site Number : 840106, Birmingham, Alabama, United States
- Barrow Neurological Institute- Site Number : 840087, Phoenix, Arizona, United States
- Phoenix Children's Hospital- Site Number : 840003, Phoenix, Arizona, United States
- University of Arizona- Site Number : 840015, Tucson, Arizona, United States
- Arkansas Childrens Hospital- Site Number : 840109, Little Rock, Arkansas, United States
- University of Arkansas for Medical Sciences- Site Number : 840113, Little Rock, Arkansas, United States
- University of California at Irvine- Site Number : 840036, Irvine, California, United States
- Loma Linda University- Genetics- Site Number : 840070, Loma Linda, California, United States
- Southern California Permanente Medical Group- Site Number : 840108, Los Angeles, California, United States
- USC Health Sciences Center Dept of Genetics- Site Number : 840082, Los Angeles, California, United States
- Children's Hospital Oakland- Site Number : 840029, Oakland, California, United States
- Children's Hospital of Orange County- Site Number : 840074, Orange, California, United States
- UC Davis MIND Institute- Site Number : 840010, Sacramento, California, United States
- University of California at San Diego- Site Number : 840007, San Diego, California, United States
- University of California at San Francisco- Site Number : 840051, San Francisco, California, United States
- +5 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT00231400 on ClinicalTrials.govOther trials for Glycogen storage disease due to acid maltase deficiency
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