CompletedPhase 2NCT00048711
Open-Label Study of Efficacy and Safety of Recombinant Human N-acetylgalactosamine 4-sulfatase in Patients With MPS VI
Studying Mucopolysaccharidosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- BioMarin Pharmaceutical
- Principal Investigator
- Stuart J Sweidler, MD, Ph.D., P.A.-CBioMarin Pharmaceutical
- Intervention
- N-acetylgalactosamine 4-sulfatase(drug)
- Eligibility
- 5 years · All sexes
- Timeline
- 2002 – 2006
Study locations (1)
- BioMarin Pharmaceutical Inc., Novato, California, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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