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14 articles matching "lung disease"

NewsRSS2 days ago

My Take on Nontraditional Medicine in Treating AATD

A patient with AATD (a rare lung disease caused by low levels of a protective protein) shares her personal experiences with complementary and alternative medicine approaches. She discusses how nontraditional treatments have fit into her overall care plan alongside standard medical treatment. The article reflects one patient's perspective on combining different types of medicine to manage her condition.

WHY IT MATTERSPatients with AATD can learn from one person's real-world experience balancing conventional treatment with complementary approaches, which may help inform their own conversations with their healthcare team about what options exist.
💬 Ask your doctorAlpha-1 Antitrypsin DeficiencyRead →
ResearchRSS3 days ago

RUNX1 gene may serve as biomarker for right heart failure in PAH

Scientists found that a gene called RUNX1 might help doctors predict when patients with pulmonary arterial hypertension (PAH) — a serious lung disease that makes it hard to pump blood — could develop heart problems. When the right side of the heart weakens in PAH patients, it becomes very dangerous. This discovery could help doctors catch and treat these heart problems earlier.

WHY IT MATTERSIf RUNX1 becomes a validated biomarker, PAH patients could receive earlier interventions to prevent right heart failure, potentially improving survival and quality of life before irreversible damage occurs.
Good to knowpulmonary arterial hypertensionright heart failureRead →
NewsRSS3 days ago

Flying High With AATD: Finding Inspiration From a Movie

A patient with AATD (Alpha-1 Antitrypsin Deficiency) found personal inspiration by watching the movie Top Gun: Maverick, discovering parallels between the fighter pilot's perseverance and their own journey managing a chronic lung disease. The article explores how popular culture can provide emotional support and motivation for people living with rare diseases. This is a personal reflection piece rather than medical news.

WHY IT MATTERSFor AATD patients, finding relatable stories and sources of inspiration in everyday media can help combat the isolation and emotional burden of managing a progressive genetic lung disease.
Good to knowAlpha-1 Antitrypsin DeficiencyRead →
NewsRSS3 days ago

Test Your Knowledge About Nerandomilast for the Treatment of PPF

This article is a quiz about nerandomilast, a medicine being studied to treat progressive pulmonary fibrosis (PPF), which is a lung disease where lung tissue becomes scarred and stiff over time, making it harder to breathe. The quiz helps patients and caregivers learn more about this potential treatment option. It's a way to test your understanding of how this medicine might help people with this serious lung condition.

WHY IT MATTERSPatients with progressive pulmonary fibrosis have limited treatment options, so learning about emerging therapies like nerandomilast helps them stay informed about potential new ways to slow lung damage.
Good to knowprogressive pulmonary fibrosisRead →
NewsRSS3 days ago

AATD on a Good Day: A Glimpse Into Life With a Rare Disease

A person who used to work as a nutrition counselor shares what it's really like to have a good day while living with AATD (alpha-1 antitrypsin deficiency). The article shows how much planning, careful decisions, and inner strength it takes to manage this rare lung disease day-to-day. Even on good days, people with AATD have to think carefully about their choices and energy levels.

WHY IT MATTERSThis firsthand account helps patients and caregivers understand that managing AATD requires constant invisible effort, which can validate their own experiences and help them feel less alone.
Good to knowAlpha-1 Antitrypsin DeficiencyRead →
AdvocacyRSS3 days ago

Artemis II reminds me to dream big for a pulmonary hypertension cure

This article uses the excitement of NASA's Artemis II space mission as inspiration to encourage big dreams about finding a cure for pulmonary hypertension, a serious lung disease that affects blood vessels. The author draws a parallel between humanity's ability to reach for the stars and the hope that patients with pulmonary hypertension should have for breakthrough treatments. The piece is motivational rather than reporting on specific medical news or research developments.

WHY IT MATTERSThis article may resonate emotionally with pulmonary hypertension patients by framing their disease journey within a larger narrative of human achievement and possibility, though it does not announce any new treatments, trials, or clinical developments.
Good to knowpulmonary hypertensionRead →
ResearchRSS3 days ago

Smartphone data may help detect rare lung disease earlier, study suggests

Researchers found that data from smartphones and wearable devices, collected over several years through a health app, can help doctors identify people with a rare lung disease called idiopathic pulmonary arterial hypertension (IPAH) earlier than before. The study used information like heart rate and activity levels from the My Heart Counts app to spot differences between people with IPAH and healthy people. This discovery could lead to faster diagnosis of this serious condition.

WHY IT MATTERSEarlier detection of IPAH could allow patients to start treatment sooner, potentially slowing disease progression and improving outcomes for this condition that currently has no cure.
Good to knowidiopathic pulmonary arterial hypertensionRead →
NewsRSS3 days ago

Growing up with PH meant answering a lot of questions from peers

A person with pulmonary hypertension (PH), a rare lung disease that makes it hard for the heart to pump blood through the lungs, shares what it was like growing up with this condition. They had to frequently miss school and explain their illness to classmates who asked questions about their absences. This article highlights the social and emotional challenges that young people with chronic rare diseases face alongside their medical treatment.

WHY IT MATTERSPatients with pulmonary hypertension and their families can find validation and community in peer experiences, while healthcare providers gain insight into the psychosocial impact of PH that extends beyond physical symptoms.
Good to knowPulmonary HypertensionRead →
AdvocacyRSS3 days ago

Guest Voice: A mother’s strength in living with pulmonary hypertension

A mother shares her personal story about being diagnosed with pulmonary hypertension three months after giving birth to her second son in 2023. The article focuses on how she manages her condition while raising three boys and the emotional impact this serious lung disease has had on her life and family.

WHY IT MATTERSPatient stories about pulmonary hypertension help newly diagnosed patients and families understand that others are managing this serious condition while maintaining family life, which can provide hope and practical insights into daily living with the disease.
Good to knowpulmonary hypertensionRead →
NewsUNITERAREApr 3

Fund Update: PAN Foundation — Idiopathic pulmonary fibrosis Fund Idiopathic pulmonary fibrosis fund is currently closed

The PAN Foundation's financial assistance program for idiopathic pulmonary fibrosis (a lung disease where lung tissue becomes scarred and stiff over time) is currently closed and is not accepting new applications. This program previously offered up to $12,000 per year to help patients pay for treatment costs. The fund status changed on April 2, 2026.

WHY IT MATTERSIf you have idiopathic pulmonary fibrosis and need help paying for medications or treatment, you cannot currently apply to this specific PAN Foundation program, so you'll need to explore other financial assistance options.
Good to knowidiopathic pulmonary fibrosisRead →
ResearchPUBMEDMar 26

Rare Pediatric Pulmonary Diseases: Insights from a Survey of Pediatric Pulmonologists in German-Speaking Countries.

Doctors who treat children with rare lung diseases in German-speaking countries were surveyed about their experience and confidence in diagnosing and treating these conditions. The study found that while common rare lung diseases like cystic fibrosis have good support systems, many other rare lung diseases don't have clear treatment guidelines. Researchers want to understand what training and resources doctors need to better help children with these uncommon lung problems.

WHY IT MATTERSIf you have a child with a rare lung disease, this research could lead to better training for pediatric lung doctors in your region, potentially reducing diagnostic delays and improving access to specialized care.
Good to knowchildhood interstitial lung diseasecongenital thoracic malformationscystic fibrosisRead →
ResearchPUBMEDMar 26

[A rare manifestation of a cystic lung disease with high suspicion of pulmonary light chain deposition disease (LCDD)].

Doctors found a rare lung disease called pulmonary light chain deposition disease (PLCDD) that creates cysts and bumps in the lungs. This disease is hard to diagnose because it looks similar to other lung conditions, but special imaging scans and blood tests for abnormal proteins can help identify it. The article explains how doctors should think about this disease when patients have unusual cyst patterns in their lungs.

WHY IT MATTERSIf you have been diagnosed with an unusual cystic lung disease that doesn't fit typical patterns, your doctor should consider testing for light chain deposition disease, which requires specific blood work and imaging to confirm.
💬 Ask your doctorpulmonary light chain deposition diseaselight chain deposition diseaseRead →
Clinical trialCLINICALTRIALSMar 26

Trial Now Recruiting: A National Registry For Pulmonary Alveolar Proteinosis (NCT02461615)

Doctors are building a national database to collect information from 500 patients with pulmonary alveolar proteinosis (PAP), a rare lung disease. This registry will help researchers better understand PAP, improve how doctors diagnose it, and test new treatments. Patients who join will have a voice in deciding what research gets done.

WHY IT MATTERSThis is an active recruitment opportunity for PAP patients to directly influence research priorities and gain access to new diagnostic tests and experimental therapies being evaluated through the registry.
You can act on thisPulmonary Alveolar ProteinosisAutoimmune Pulmonary Alveolar ProteinosisRead →
ResearchCLINICALTRIALSMar 26

Trial Now Recruiting: Human Biospecimen Procurement Protocol: Biorepository to Support Translational Research to Identify Disease Mechanism(s) (NCT02543996)

Researchers at the National Heart, Lung, and Blood Institute are collecting blood and tissue samples from up to 10,000 people to study rare genetic diseases. They want to understand what causes these diseases by examining the samples in a lab. People of any age with undiagnosed or heart and lung diseases can participate. Samples can be collected at the NIH Clinical Center or through your own doctor.

WHY IT MATTERSThis biorepository is actively recruiting and could help researchers identify the genetic causes of your undiagnosed condition, potentially leading to better treatments and diagnosis methods for rare diseases.
You can act on thisUndiagnosed DiseasesRare Genetic DiseasesCardiovascular DiseaseRead →

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