Rare bone development disorder

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ORPHA:139012
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16Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Orphanet code 139012 refers to a rare bone development disorder, but this specific entry corresponds to a condition with very limited published clinical data and no well-established ICD-10 classification. Rare bone development disorders in this category generally affect how bones grow, form, and maintain their structure. These conditions can lead to bones that are unusually shaped, too fragile, too dense, or that do not grow to their expected size. Symptoms often become apparent during childhood or even at birth, depending on the severity of the condition. Patients with rare bone development disorders may experience frequent fractures, short stature, limb deformities, joint problems, and chronic pain. Some forms can also affect the skull, spine, and rib cage, which may lead to breathing difficulties or neurological complications. The treatment landscape for most rare bone disorders focuses on managing symptoms rather than curing the underlying cause. This may include orthopedic surgery, physical therapy, pain management, and in some cases medications that target bone metabolism. Genetic counseling is often recommended for affected families to understand the inheritance pattern and recurrence risk. Because this specific Orphanet entry (139012) has limited detailed clinical characterization in the medical literature, patients and families are encouraged to work closely with a clinical geneticist and bone specialist to obtain an accurate diagnosis and personalized care plan.

Also known as:

Key symptoms:

Abnormal bone shape or structureFrequent bone fracturesShort stature or growth problemsLimb deformitiesJoint stiffness or limited range of motionChronic bone or joint painDifficulty walking or movingSpinal curvature or abnormalitiesDelayed motor milestones

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Rare bone development disorder.

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No actively recruiting trials found for Rare bone development disorder at this time.

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Specialists

16 foundView all specialists →
MM
Michael Beck, MD
Specialist
PI on 1 active trial
JM
Jiri Zeman, MD
Specialist
PI on 1 active trial
AM
Alessandro Pini, MD
San Donato Milanese, Lombardy
Specialist

Rare Disease Specialist

PI on 3 active trials
CM
Carlos R Ferreira Lopez, M.D.
Bethesda, Maryland
Specialist

Rare Disease Specialist

PI on 2 active trials
LP
Luca Sangiorgi, MD, PhD
Bologna, Emilia-Romagna
Specialist

Rare Disease Specialist

PI on 2 active trials
SM
Sarthak Gupta, M.D.
Bethesda, Maryland
Specialist

Rare Disease Specialist

PI on 1 active trial
RP
Raajit Rampal, MD, PhD
Chicago, Illinois
Specialist

Rare Disease Specialist

PI on 4 active trials
ZM
Zagorka Pejin, MD
Specialist
PI on 1 active trial
RP
Rosanna Cardani, PhD
San Donato Milanese, Milan
Specialist

Rare Disease Specialist

PI on 1 active trial
GM
Giuliana Trifirò, MD
San Donato Milanese, Lombardy
Specialist

Rare Disease Specialist

PI on 1 active trial1 Rare bone development disorder publication

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Rare bone development disorder.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Rare bone development disorder

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What is the exact name and genetic cause of my or my child's bone disorder?,What is the expected course of this condition over time?,Are there any specific treatments or medications that could help strengthen the bones?,How often should we have follow-up imaging and specialist visits?,Are there activities or sports that should be avoided to reduce fracture risk?,Should other family members be tested for this condition?,Are there any clinical trials or new therapies being studied for this condition?

Common questions about Rare bone development disorder

What is Rare bone development disorder?

Orphanet code 139012 refers to a rare bone development disorder, but this specific entry corresponds to a condition with very limited published clinical data and no well-established ICD-10 classification. Rare bone development disorders in this category generally affect how bones grow, form, and maintain their structure. These conditions can lead to bones that are unusually shaped, too fragile, too dense, or that do not grow to their expected size. Symptoms often become apparent during childhood or even at birth, depending on the severity of the condition. Patients with rare bone development

Which specialists treat Rare bone development disorder?

16 specialists and care centers treating Rare bone development disorder are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.