Primary lateral sclerosis

Last reviewed

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ORPHA:35689OMIM:611637G12.2
Who is this for?
Show terms as
2Active trials25Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Primary lateral sclerosis, often called PLS, is a rare neurological disease that affects the nerve cells in the brain that control voluntary movement. These nerve cells, called upper motor neurons, gradually stop working properly. Unlike the more well-known ALS (amyotrophic lateral sclerosis), PLS does not typically affect the lower motor neurons — the nerve cells in the spinal cord that directly connect to muscles. This difference is important because it means PLS usually progresses more slowly and does not shorten life expectancy as dramatically as ALS. The main symptoms of PLS include slowly worsening stiffness and weakness in the legs, arms, and sometimes the face and throat. People may notice they have trouble walking, balancing, or speaking clearly. Muscle spasms and cramps are also common. Symptoms usually begin in the legs and gradually spread upward over many years. There is currently no cure for PLS. Treatment focuses on managing symptoms and maintaining quality of life. Physical therapy, occupational therapy, and medications to reduce muscle stiffness are the main tools doctors use. With the right support, many people with PLS live for decades after diagnosis and can maintain meaningful independence for a long time.

Also known as:

Key symptoms:

Stiffness and tightness in the legs (spasticity)Slowly worsening leg weaknessDifficulty walking and problems with balanceMuscle cramps and spasmsWeakness or stiffness spreading to the arms over timeSlurred or slow speechDifficulty swallowingEmotional changes such as sudden laughing or crying (pseudobulbar affect)FatigueDragging one or both feet when walkingStiffness in the hands and fingers

Clinical phenotype terms (26)— hover any for plain English
Generalized hyperreflexiaHP:0007034Pseudobulbar signsHP:0002200Loss of speechHP:0002371Abnormal upper motor neuron morphologyHP:0002127Progressive spastic paraparesisHP:0007199Impaired smooth pursuitHP:0007772Weakness due to upper motor neuron dysfunctionHP:0010549Hoffmann signHP:0031993Atrophy of the spinal cordHP:0006827
Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗OMIM ↗NORD ↗

FDA & Trial Timeline

2 events
Mar 2016Use of Dalfampridine in Primary Lateral Sclerosis

Hospital for Special Surgery, New York — PHASE1

TrialACTIVE NOT RECRUITING
Sep 2015Imaging Biomarkers in ALS

University of Minnesota

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Primary lateral sclerosis.

2 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

2 recruitingView all trials with filters →
Phase 11 trial
Use of Dalfampridine in Primary Lateral Sclerosis
Phase 1
Active
PI: Dale Lange, MD (HSS) · Sites: Gainesville, Florida; Boston, Massachusetts +1 more · Age: 1899 yrs
Other1 trial
Imaging Biomarkers in ALS
Actively Recruiting
PI: David Walk, MD (University of Minnesota) · Sites: Minneapolis, Minnesota · Age: 2175 yrs

Specialists

25 foundView all specialists →
MP
Maurizio Inghilleri, Prof
Specialist
PI on 1 active trial
MM
Merit Cudkowicz, M.D., MSc
BOSTON, MA
Specialist
PI on 1 active trial
TM
Ted M Burns, MD
LINCOLN, NE
Specialist
PI on 1 active trial
GP
Gaelle Bruneteau, MD, PhD
Specialist
PI on 2 active trials
JP
Jeremy Shefner, MD, PhD
PHOENIX, AZ
Specialist
PI on 3 active trials
RP
Richard S Bedlack, MD, PhD
DURHAM, NC
Specialist
PI on 2 active trials
SY
Shan Ye
SAN FRANCISCO, CA
Specialist
PI on 2 active trials
JM
Jinsy Andrews, MD
NEW YORK, NY
Specialist
PI on 1 active trial
SM
Sanne Piepers, MD
Specialist
PI on 1 active trial
NM
Najeebah Abdul-Musawir, MD,MBA
Specialist
PI on 2 active trials
SM
Sonja W De Jong, MD
Specialist
PI on 1 active trial
JP
Jennifer L Collinger, PhD
Specialist
PI on 2 active trials
VP
Vincent Meininger, MD, PhD
Specialist
PI on 1 active trial
SP
Soo-Yeon Kim, PhD
Specialist
PI on 1 active trial
TL
Thierry Lagarde
Specialist
PI on 1 active trial
JP
Jimin Lee, Ph.D.
Specialist
PI on 1 active trial
NP
Navin Viswanathan, Ph.D.
Specialist
PI on 1 active trial
AP
Anne Olmstead, Ph.D.
YPSILANTI, MI
Specialist
PI on 1 active trial
NM
nuria alegret, MD
Specialist
PI on 1 active trial
MM
Michael Harrison, MD
Specialist
PI on 1 active trial
MM
Mohammed Sanjak, PhD, PT, MBA
Specialist
PI on 1 active trial
DW
David Walk
MINNEAPOLIS, MN
Specialist
PI on 1 active trial
EL
Eduardo Locatelli
FORT LAUDERDALE, FL
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Primary lateral sclerosis.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Primary lateral sclerosis

Disease timeline:

New recruiting trial: Imaging Biomarkers in ALS

A new clinical trial is recruiting patients for Primary lateral sclerosis

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.How confident are you in the PLS diagnosis, and what would make you reconsider it?,How often should I be monitored, and what signs should prompt me to contact you sooner?,Is there any chance my PLS could develop into ALS, and how would we know?,What medications or therapies do you recommend to manage my muscle stiffness right now?,Should I have genetic testing, and could this condition affect my family members?,What therapists or specialists should be part of my care team?,Are there any clinical trials for PLS that I might be eligible to join?

Common questions about Primary lateral sclerosis

What is Primary lateral sclerosis?

Primary lateral sclerosis, often called PLS, is a rare neurological disease that affects the nerve cells in the brain that control voluntary movement. These nerve cells, called upper motor neurons, gradually stop working properly. Unlike the more well-known ALS (amyotrophic lateral sclerosis), PLS does not typically affect the lower motor neurons — the nerve cells in the spinal cord that directly connect to muscles. This difference is important because it means PLS usually progresses more slowly and does not shorten life expectancy as dramatically as ALS. The main symptoms of PLS include slow

How is Primary lateral sclerosis inherited?

Primary lateral sclerosis follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Primary lateral sclerosis typically begin?

Typical onset of Primary lateral sclerosis is adult. Age of onset can vary across affected individuals.

Are there clinical trials for Primary lateral sclerosis?

Yes — 2 recruiting clinical trials are currently listed for Primary lateral sclerosis on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Primary lateral sclerosis?

25 specialists and care centers treating Primary lateral sclerosis are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.