Myelodysplastic/myeloproliferative disease

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ORPHA:98275
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2FDA treatments4Active trials29Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Also known as:

MDSMyelodysplastic syndromes
Orphanet ↗NORD ↗

FDA & Trial Timeline

9 events
Apr 2026

IMATINIB MESYLATE: New indication approved

FDAcompleted
Jan 2026GLEEVEC: New indication approved
FDAcompleted
Nov 2024A Multicenter Study on the Treatment of MDS/MPN Overlap Syndrome With AZA or Rux Combined With Selinexor

Peking Union Medical College Hospital — PHASE2

TrialENROLLING BY INVITATION
Jun 2024MYELOMATCH: A Screening Study to Assign People With Myeloid Cancer to a Treatment Study or Standard of Care Treatment Within myeloMATCH (MyeloMATCH Screening Trial)

National Cancer Institute (NCI) — PHASE2

TrialRECRUITING
May 2024Sorafenib Relapase Prophylaxis After HCT With PTBCy Regimen

St. Petersburg State Pavlov Medical University — PHASE2

TrialRECRUITING
Jan 2023

IMATINIB MESYLATE: New indication approved

FDAcompleted
Nov 2022A Study Using Subject-specific MRD to Adopt Treatment After HSCT for Subjects With MDS

Karolinska University Hospital — PHASE2

TrialRECRUITING
Dec 2020CPX-351 and Ivosidenib for the Treatment of IDH1 Mutated Acute Myeloid Leukemia or High-Risk Myelodysplastic Syndrome

M.D. Anderson Cancer Center — PHASE2

TrialRECRUITING
Jul 2020

IMATINIB MESYLATE: FDA approved

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

2 available

Imatinib Mesylate

IMATINIB MESYLATE· Apotex Corp

Adult patients with myelodysplastic/myeloproliferative diseases (MDS/MPD) associated with platelet-derived growth factor receptor (PDGFR) gene re-arrangements

View Details →FDA Label ↗

Imkeldi

IMATINIB ORAL· Shorla Oncology Inc.,

Adult patients with myelodysplastic/myeloproliferative diseases (MDS/MPD) associated with platelet-derived growth factor receptor (PDGFR) gene re-arrangements.

View Details →FDA Label ↗

Clinical Trials

4 recruitingView all trials with filters →
Phase 24 trials
MYELOMATCH: A Screening Study to Assign People With Myeloid Cancer to a Treatment Study or Standard of Care Treatment Within myeloMATCH (MyeloMATCH Screening Trial)
Phase 2
Actively Recruiting
PI: Jerald P Radich (SWOG Cancer Research Network) · Sites: Birmingham, Alabama; Phoenix, Arizona +330 more · Age: 18–99 yrs
View on ClinicalTrials.gov ↗I'm interested →
CPX-351 and Ivosidenib for the Treatment of IDH1 Mutated Acute Myeloid Leukemia or High-Risk Myelodysplastic Syndrome
Phase 2
Actively Recruiting
PI: Courtney DiNardo, MD (M.D. Anderson Cancer Center) · Sites: Houston, Texas · Age: 18–99 yrs
View on ClinicalTrials.gov ↗I'm interested →
A Study Using Subject-specific MRD to Adopt Treatment After HSCT for Subjects With MDS
Phase 2
Actively Recruiting
PI: Magnus Tobiasson, PhD (Karolinska University Hospital) · Sites: Stockholm · Age: 18–99 yrs
View on ClinicalTrials.gov ↗I'm interested →
Sorafenib Relapase Prophylaxis After HCT With PTBCy Regimen
Phase 2
Actively Recruiting
· Sites: Saint Petersburg · Age: 18–75 yrs
View on ClinicalTrials.gov ↗I'm interested →

Specialists

Showing 25 of 29View all specialists →
SM
Sanjay Mohan, MD
NEW YORK, NY
Specialist
PI on 3 active trials
HM
Hagop Kantarjian, MD
HOUSTON, TX
Specialist
PI on 7 active trials
MM
Minocher Battiwalla, MD
NASHVILLE, TN
Specialist
PI on 2 active trials
FR
Farhad Ravandi-Kashani
HOUSTON, TX
Specialist
PI on 7 active trials2 Myelodysplastic/myeloproliferative disease publications
CM
Corey Cutler, MD, MPH
PARK CITY, UT
Specialist
PI on 3 active trials
FM
Farhad Ravandi-Kashani, MD
HOUSTON, TX
Specialist
PI on 8 active trials
AM
Abhay Singh, MD, MPH
Cleveland, Ohio
Specialist

Rare Disease Specialist

PI on 1 active trial
BS
Bart Scott
SEATTLE, WA
Specialist
PI on 3 active trials
TM
Thomas G. Martin, MD
Specialist
PI on 4 active trials
CD
Colleen Delaney
OLD GREENWICH, CT
Specialist
PI on 3 active trials
MS
Mikkael A Sekeres
MIAMI, FL
Specialist
PI on 1 active trial3 Myelodysplastic/myeloproliferative disease publications
SM
Steven Devine, MD
LA CROSSE, WI
Specialist
PI on 4 active trials
GM
Guillermo M Bravo, MD
CHANDLER, AZ
Specialist
PI on 1 active trial1 Myelodysplastic/myeloproliferative disease publication
SM
Susan K. Parsons, MD, MRP
Specialist
PI on 1 active trial
FG
Francis Giles
SAN ANTONIO, TX
Specialist
PI on 4 active trials
CD
Christopher Dvorak
AURORA, IL
Specialist
PI on 1 active trial
CP
Claudio G. Brunstein, MD, PhD
MINNEAPOLIS, MN
Specialist
PI on 6 active trials
MM
Margaret L. MacMillan, MD
Specialist
PI on 4 active trials
JM
James N Kochenderfer, M.D.
BETHESDA, MD
Specialist
PI on 6 active trials
MM
Mignon Loh, MD
SAN FRANCISCO, CA
Specialist
PI on 2 active trials
ZM
Zaid Al Kadhimi, MD
Specialist
PI on 1 active trial
RM
Raphaël Itzykson, MD
Specialist
PI on 1 active trial
PP
Pierre Fenaux, MD, PHD
Specialist
PI on 1 active trial
JD
Jürgen Wehmeyer, Dr.
Specialist
PI on 1 active trial
OG
Olga Gurevitch
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center ↗

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center ↗

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program ↗

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site ↗

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site ↗

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site ↗

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine ↗

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program ↗

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Myelodysplastic/myeloproliferative disease.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Myelodysplastic/myeloproliferative disease

Disease timeline:

New recruiting trial: A Study Using Subject-specific MRD to Adopt Treatment After HSCT for Subjects With MDS

A new clinical trial is recruiting patients for Myelodysplastic/myeloproliferative disease

New recruiting trial: Sorafenib Relapase Prophylaxis After HCT With PTBCy Regimen

A new clinical trial is recruiting patients for Myelodysplastic/myeloproliferative disease

New recruiting trial: CPX-351 and Ivosidenib for the Treatment of IDH1 Mutated Acute Myeloid Leukemia or High-Risk Myelodysplastic Syndrome

A new clinical trial is recruiting patients for Myelodysplastic/myeloproliferative disease

New recruiting trial: Autologous T Cells Transduced With Retroviral Vectors Expressing TCRs for Participant-specific Neoantigens in Patients With Hematologic Malignancies

A new clinical trial is recruiting patients for Myelodysplastic/myeloproliferative disease

New recruiting trial: MYELOMATCH: A Screening Study to Assign People With Myeloid Cancer to a Treatment Study or Standard of Care Treatment Within myeloMATCH (MyeloMATCH Screening Trial)

A new clinical trial is recruiting patients for Myelodysplastic/myeloproliferative disease

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Myelodysplastic/myeloproliferative disease

Are there clinical trials for Myelodysplastic/myeloproliferative disease?

Yes — 4 recruiting clinical trials are currently listed for Myelodysplastic/myeloproliferative disease on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Myelodysplastic/myeloproliferative disease?

25 specialists and care centers treating Myelodysplastic/myeloproliferative disease are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Myelodysplastic/myeloproliferative disease?

1 patient support program are currently tracked on UniteRare for Myelodysplastic/myeloproliferative disease. See the treatments and support programs sections for copay assistance, eligibility, and contact details.