Juvenile idiopathic inflammatory myopathy

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15Specialists8Treatment centers

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Overview

Juvenile idiopathic inflammatory myopathy (JIIM) is a group of rare autoimmune diseases that primarily affect children and teenagers, causing inflammation in the muscles and sometimes the skin. The most common forms include juvenile dermatomyositis and juvenile polymyositis. In these conditions, the body's immune system mistakenly attacks its own healthy muscle tissue, leading to muscle weakness, pain, and fatigue. When the skin is involved, children may develop distinctive rashes, particularly a purplish discoloration around the eyes or over the knuckles. The disease typically causes weakness in the muscles closest to the trunk of the body, such as the thighs, upper arms, neck, and trunk. Children may have trouble climbing stairs, getting up from the floor, lifting their arms, or holding their head up. Some children also develop calcium deposits under the skin (calcinosis), difficulty swallowing, or lung problems. In rare cases, blood vessels throughout the body can become inflamed. Treatment focuses on suppressing the overactive immune system and reducing inflammation. First-line therapy usually involves high-dose corticosteroids such as prednisone, often combined with other immunosuppressive medications like methotrexate. Intravenous immunoglobulin (IVIG) is also commonly used. Physical therapy plays a critical role in maintaining muscle strength and function. With early and aggressive treatment, many children achieve remission or significant improvement, though some may have a chronic relapsing course.

Also known as:

Key symptoms:

Muscle weakness, especially in the thighs and upper armsDifficulty climbing stairs or getting up from the floorPurplish or reddish rash around the eyes (heliotrope rash)Red or scaly bumps over the knuckles (Gottron papules)Fatigue and low energyMuscle pain or tendernessDifficulty swallowingDifficulty raising arms above the headCalcium deposits under the skin (hard lumps)FeverJoint pain or swellingSkin ulcersHoarse or nasal-sounding voiceShortness of breathBelly pain

Inheritance

Multifactorial

Caused by a mix of several genes and environmental factors

Age of Onset

Juvenile

Begins in the teen years

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Juvenile idiopathic inflammatory myopathy.

View clinical trials →

No actively recruiting trials found for Juvenile idiopathic inflammatory myopathy at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Juvenile idiopathic inflammatory myopathy community →

Specialists

15 foundView all specialists →
AM
Ann M. Reed, MD
Specialist
PI on 1 active trial1 Juvenile idiopathic inflammatory myopathy publication
CM
Chester V. Oddis, MD
PITTSBURGH, PA
Specialist
PI on 2 active trials
LM
Laura Schanberg, MD
DURHAM, NC
Specialist
PI on 2 active trials
AM
Adam I Schiffenbauer, M.D.
WASHINGTON, DC
Specialist
PI on 4 active trials
GP
Guy Berbers, PhD
Specialist
PI on 1 active trial
LM
Lisa G Rider, M.D.
AURORA, CO
Specialist
PI on 4 active trials
CM
Christy Sandborg, MD
PALO ALTO, CA
Specialist
PI on 1 active trial
CM
Carol Wallace, MD
Specialist
PI on 1 active trial
FP
Fiona van der KLis, MD, PhD
Specialist
PI on 1 active trial
NP
Nico M Wulffraat, MD, PhD
Specialist
PI on 1 active trial
NM
Norman T Illowite, MD
Specialist
PI on 1 active trial
SP
Susmita Kashikar-Zuck, PhD
CINCINNATI, OH
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Juvenile idiopathic inflammatory myopathy.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Juvenile idiopathic inflammatory myopathy

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What type of juvenile inflammatory myopathy does my child have, and how severe is it?,What medications will be used, and what are the possible side effects we should watch for?,How often will my child need blood tests and follow-up visits?,What physical activities are safe, and should we start physical therapy right away?,What are the signs of a disease flare, and when should we seek urgent care?,Are there any clinical trials or newer treatments available for my child?,What is the long-term outlook, and what complications should we be aware of?

Common questions about Juvenile idiopathic inflammatory myopathy

What is Juvenile idiopathic inflammatory myopathy?

Juvenile idiopathic inflammatory myopathy (JIIM) is a group of rare autoimmune diseases that primarily affect children and teenagers, causing inflammation in the muscles and sometimes the skin. The most common forms include juvenile dermatomyositis and juvenile polymyositis. In these conditions, the body's immune system mistakenly attacks its own healthy muscle tissue, leading to muscle weakness, pain, and fatigue. When the skin is involved, children may develop distinctive rashes, particularly a purplish discoloration around the eyes or over the knuckles. The disease typically causes weaknes

How is Juvenile idiopathic inflammatory myopathy inherited?

Juvenile idiopathic inflammatory myopathy follows a multifactorial inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Juvenile idiopathic inflammatory myopathy typically begin?

Typical onset of Juvenile idiopathic inflammatory myopathy is juvenile. Age of onset can vary across affected individuals.

Which specialists treat Juvenile idiopathic inflammatory myopathy?

15 specialists and care centers treating Juvenile idiopathic inflammatory myopathy are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.