RecruitingPhase 1NCT06996756
Gene Therapy for Alpha 1- Antitrypsin Deficiency
Studying Alpha-1-antitrypsin deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Weill Medical College of Cornell University
- Principal Investigator
- Ronald G Crystal, MDWeill Medical College of Cornell University
- Intervention
- AAV8hAAT(AVL)(biological)
- Enrollment
- 16 enrolled
- Eligibility
- 18-70 years · All sexes
- Timeline
- 2025 – 2032
Study locations (1)
- WCMC Department of Genetic Medicine, New York, New York, United States
Collaborators
National Heart, Lung, and Blood Institute (NHLBI)
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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