Active, not recruitingPhase 1NCT06738017
Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult Participants
Studying Alpha-1-antitrypsin deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- BioMarin Pharmaceutical
- Principal Investigator
- Medical Director, MDBioMarin Pharmaceutical
- Intervention
- BMN 349(drug)
- Enrollment
- 6 enrolled
- Eligibility
- 18-75 years · All sexes
- Timeline
- 2025 – 2025
Study locations (8)
- University of California, San Diego, San Diego, California, United States
- Saint Louis University, St Louis, Missouri, United States
- Medpace Clinical Pharmacology Unit, Cincinnati, Ohio, United States
- The Medical University of South Carolina, Charleston, South Carolina, United States
- NHS Lothian, Edinburgh, UK, United Kingdom
- Royal Free London NHS Foundation Trust, London, UK, United Kingdom
- Nottingham University Hospitals, Nottingham, UK, United Kingdom
- University Hospital Southampton NHS Foundation Trust, Southampton, UK, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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