RecruitingPhase 3NCT06971094
Safety and Efficacy Evaluation of GC101 Gene Therapy Via Intrathecal (IT) Injectionin the Treatment of Patients With Type 2 Spinal Muscular Atrophy (SMA) - Phase III
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- GeneCradle Inc
- Principal Investigator
- GeneCradle, Inc China
- Intervention
- GC101 adeno-associated virus injection(genetic)
- Enrollment
- 50 enrolled
- Eligibility
- 2-12 years · All sexes
- Timeline
- 2025 – 2026
Study locations (7)
- The Seventh Medical Center of Chinese PLA General Hospital, Beijing, China
- Children's Medical Center of Peking University First Hospital, Beijing, China
- Beijing Children's Hospital, Capital Medical University, Beijing, China
- National Children's Medical Center，Shanghai Jiaotong University, Shanghai, China
- Shenzhen Children's Hospital, Shenzhen, China
- Children's Hospital of Soochow University, Suzhou, China
- Wuhan Children's Hospital, Tongji Medical College, Huazhong University of Science & Technology, Wuhan, China
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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