RecruitingNCT06532474
Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- St. Jude Children's Research Hospital
- Principal Investigator
- Richard Finkel, MDSt. Jude Children's Research Hospital
- Enrollment
- 24 enrolled
- Eligibility
- 5-20 years · All sexes
- Timeline
- 2025 – 2027
Study locations (1)
- St. Jude Children's Research Hospital, Memphis, Tennessee, United States
Collaborators
Genentech, Inc.
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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