RecruitingPhase 2NCT07287982
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- argenx
- Intervention
- ARGX-119 IV(biological)
- Enrollment
- 60 enrolled
- Eligibility
- 5-17 years · All sexes
- Timeline
- 2025 – 2029
Study locations (17)
- Arkansas Children's Hospital, Little Rock, Arkansas, United States
- Rady Childrens Hospital, San Diego, California, United States
- Stanford University Medical Center, Stanford, California, United States
- Connecticut Children's Medical Center, Hartford, Connecticut, United States
- Rare Disease Research FL LLC, Kissimmee, Florida, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- University of Iowa Stead Family Children's Hospital, Iowa City, Iowa, United States
- The Johns Hopkins Hospital, Baltimore, Maryland, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- The Curators of the University of Missouri on behalf of University of Missouri Health Care, Columbia, Missouri, United States
- Columbia University Herbert Irving Comprehensive Cancer Center, New York, New York, United States
- Rare Disease Research NC, LLC, Hillsborough, North Carolina, United States
- Children's Hospital Philadelphia - Neurology, Philadelphia, Pennsylvania, United States
- St. Jude Children's Research Hospital, Memphis, Tennessee, United States
- Neurology Rare Disease Center, Flower Mound, Texas, United States
- +2 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT07287982 on ClinicalTrials.govOther trials for Spinal Muscular Atrophy
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