Enrolling by invitationNCT06588803
A Long-term Follow-up Study Evaluating Intravenous Injection of EXG001-307 in Patients With Type 1 SMA
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Guangzhou Jiayin Biotech Ltd
- Principal Investigator
- YI WANG, Ph D.Children's Hospital of Fudan University
- Intervention
- No intervention, only for observational studies(other)
- Enrollment
- 18 enrolled
- Eligibility
- All sexes
- Timeline
- 2025 – 2030
Study locations (1)
- The Children's Hospital of Fudan University, Shanghai, Shanghai Municipality, China
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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