RecruitingPHASE1, PHASE2NCT06421831
Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- GeneCradle Inc
- Intervention
- GC101(genetic)
- Enrollment
- 21 enrolled
- Eligibility
- 2 years · All sexes
- Timeline
- 2024 – 2028
Study locations (1)
- Beijing Tiantan Hospital, Capital Medical University, Beijing, Beijing Municipality, China
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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