RecruitingNot applicableNCT06321965
Characterization of New Phenotypes of Patients With Spinal Muscular Atrophy Treated With SMN Restoring Therapy
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Hospices Civils de Lyon
- Principal Investigator
- Laure LE GOFF, PI
- Intervention
- evaluation of muscle function(other)
- Enrollment
- 60 enrolled
- Eligibility
- 0-16 years · All sexes
- Timeline
- 2024 – 2029
Study locations (8)
- Pediatric Rehabilitation Service - L'Escale Mother and Child Hospital, Bron, Rhone, France
- CHRU of Brest, Brest, France
- Pediatric Neurology and Resuscitation Raymond-Poincare Hospital, Garche, France
- Pediatric Neurology Swynghedauw Hospital, Lille, France
- Marseille University Hospital - Timone Hospital Department of Pediatric Neurology - Specialized Pediatrics and Child Medicine, Marseille, France
- I-Motion Pediatric Clinical Trial Platform Armand Trousseau Hospital, Paris, France
- Hautepierre Hospital - Mother and Child Hospital, Strasbourg, France
- Department of Pediatrics - Neurology and Infectious Diseases Toulouse University Hospital - Children's Hospital, Toulouse, France
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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